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authFullName_s : Martina Kropp
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Engineering of PEDF-Expressing Primary Pigment Epithelial Cells by the SB Transposon System Delivered by pFAR4 Plasmids

Gabriele Thumann , Nina Harmening , Cecile Prat-Souteyrand , Corinne Marie , Marie Pastor et al.
Molecular Therapy - Nucleic Acids, 2017, 6, pp.302-314. ⟨10.1016/j.omtn.2017.02.002⟩
Journal articles hal-03292053v1
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The Antibiotic-free pFAR4 Vector Paired with the Sleeping Beauty Transposon System Mediates Efficient Transgene Delivery in Human Cells

Marie Pastor , Sandra Johnen , Nina Harmening , Mickael Quiviger , Julie Pailloux et al.
Molecular Therapy - Nucleic Acids, 2018, 11, pp.57-67. ⟨10.1016/j.omtn.2017.12.017⟩
Journal articles hal-03292039v1
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Preclinical Evaluation of a Cell-Based Gene Therapy Using the Sleeping Beauty Transposon System in Choroidal Neovascularization

Maria Hernandez , Sergio Recalde , Laura Garcia-Garcia , Jaione Bezunartea , Csaba Miskey et al.
Molecular Therapy - Methods and Clinical Development, 2019, 15, pp.403-417. ⟨10.1016/j.omtm.2019.10.013⟩
Journal articles hal-03292059v1
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Long-Term PEDF Release in Rat Iris and Retinal Epithelial Cells after Sleeping Beauty Transposon-Mediated Gene Delivery

Laura Garcia-Garcia , Sergio Recalde , Maria Hernandez , Jaione Bezunartea , Juan Roberto Rodriguez-Madoz et al.
Molecular Therapy - Nucleic Acids, 2017, 9, ⟨10.1016/j.omtn.2017.08.001⟩
Journal articles hal-03292049v1