Chem-AAV: Chemically Modified AAV for Gene Therapy
Mathieu Mevel
,
Mohammed Bouzelha
,
Laurence Dubreil
,
Estelle Toublanc
,
Veronique Blouin
et al.
20th Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy , 2017, NA, France. pp.1
Conference papers
hal-01600854v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
La génétique, science humaine
Muriel Fabre Magnan
,
Philippe Moullier
Belin, 303 p., 2004
Books
hal-00425206v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Off-Target Analysis of a rAAV-U7snRNA Vector Used for the Treatment of Duchenne Patients By Exon Skipping
Claire Domenger
,
Aurélie Lardenois
,
Marine Allais
,
Virginie Francois
,
Marie Montus
et al.
18. Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) , American Society of Cell and Gene Therapy (ASGCT). Milwaukee, USA., May 2015, Nouvelle Orléans, United States. pp.1
Conference papers
hal-02740856v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Saut d’exon par AAV8/U7 dans la dystrophie musculaire de Duchenne : De la souris à l’homme en passant par le chien
Laurent Servais
,
Caroline Le Guiner
,
Marie Montus
,
Luis Garcia
,
Yves Fromes
et al.
XXIIème congrès de la SFNP , Société Française de Neurologie Pédiatrique (SFNP). FRA., Jan 2012, Marseille, France
Conference papers
hal-02804793v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Human alpha-Iduronidase Gene Transfer Mediated by Adeno-Associated Virus Types 1, 2, and 5 in the Brain of Nonhuman Primates: Vector Diffusion and Biodistribution
Carine Ciron
,
Arnaud Cressant
,
Françoise Roux
,
Sylvie Raoul
,
Yan Cherel
et al.
Journal articles
hal-02663855v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Chemical modification of the adeno-associated virus capsid to improve gene delivery
Mathieu Mével
,
Mohammed Bouzelha
,
Aurélien Leray
,
Simon Pacouret
,
Mickaël Guilbaud
et al.
Journal articles
inserm-02451454v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Effective Limb Transduction and Phenotypic Correction after Injection of rAAV8-U7 snRNA in GRMD Dogs
Caroline Le Guiner
,
Marie Montus
,
Laurent Servais
,
Luis Garcia
,
Yves Fromes
et al.
ASGCT Translational Science Training Course , American Society of Cell and Gene Therapy (ASGCT). USA., Mar 2011, Seattle, United States. pp.332
Conference papers
hal-01191233v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Advanced Characterization of DNA Molecules in rAAV Vector Preparations by Single-stranded Virus Next-generation Sequencing
Emilie Lecomte
,
Benoit Tournaire
,
Benjamin Cogné
,
Jean-Baptiste Dupont
,
Pierre Lindenbaum
et al.
Journal articles
inserm-01799968v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy
Caroline C. Le Guiner
,
Laurent Servais
,
Marie Montus
,
Thibaut Thibaut
,
Bodvael Fraysse
et al.
Journal articles
hal-02179396v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Gene Therapy Prolongs Survival and Restores Function in Murine and Canine Models of Myotubular Myopathy
Martin Childers
,
Romain Joubert
,
Karine Poulard
,
Christel Moal
,
Robert Grange
et al.
Journal articles
hal-02180848v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Characterization of Producer Cell-Dependent Restriction of Murine Leukemia Virus Replication
Fatima Serhan
,
Nathalie Jourdan
,
Sylvie Saleun
,
Philippe Moullier
,
Ghislaine Duisit
et al.
Journal articles
hal-03975585v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Mannose-coupled AAV2: a second generation AAV vector for increased retinal gene therapy efficiency
Mathieu Mével
,
Virginie Pichard
,
Mohammed Bouzelha
,
Dimitri Alvarez-Dorta
,
Pierre-Alban Lalys
et al.
2022
Preprints, Working Papers, ...
hal-03860614v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Successful Gene Therapy in the RPGRIP1-deficient Dog: a Large Model of Cone-Rod Dystrophy.
Elsa Lhériteau
,
Lolita Petit
,
Michel Weber
,
Guylène Le Meur
,
Jack-Yves Deschamps
et al.
Journal articles
hal-00957330v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
In Vivo Delivery of Human α - l -Iduronidase in Mice Implanted with Neo-Organs
Anna Salvetti
,
Philippe Moullier
,
Véronique Cornet
,
Doug Brooks
,
John Hopwood
et al.
Journal articles
hal-03330129v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Safety and Long-Term Efficacy of AAV4 Gene Therapy in Patients with RPE65 Leber Congenital Amaurosis
Guylène Le Meur
,
Pierre Lebranchu
,
Fanny Billaud
,
Oumeya Adjali
,
Sébastien Schmitt
et al.
Journal articles
inserm-01785885v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Tetramer-Based Enrichment of Preexisting Anti-AAV8 CD8 + T Cells in Human Donors Allows the Detection of a T EMRA Subpopulation
Celine Vandamme
,
Rebecca Xicluna
,
Leslie Hesnard
,
Marie Devaux
,
Nicolas Jaulin
et al.
Journal articles
inserm-02447186v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Retroviral-mediated gene transfer corrects very-long-chain fatty acid metabolism in adrenoleukodystrophy fibroblasts.
Nathalie Cartier
,
Jacqueline Lopez
,
Philippe Moullier
,
Francis Rocchiccioli
,
Marie-Odile Rolland
et al.
Proceedings of the National Academy of Sciences of the United States of America , 1995, 92 (5), pp.1674-1678.
⟨10.1073/pnas.92.5.1674⟩
Journal articles
hal-03834875v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Delivery of therapeutic proteins from genetically-modified cells
Nadia Naffakh
,
Philippe Moullier
,
Anna Salvetti
,
Delphine Bohl
,
Olivier Danos
et al.
Journal articles
hal-03330125v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Intravenous Administration of Self-complementary AAV9 Enables Transgene Delivery to Adult Motor Neurons
Sandra Duqué
,
Béatrice Joussemet
,
Christel Rivière
,
Thibaut Marais
,
Laurence Dubreil
et al.
Journal articles
hal-02666576v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Accurate Identification and Quantification of DNA Species by Next Generation Sequencing in Adeno-Associated Viral Vectors Produced in Insect Cells
Magalie Penaud-Budloo
,
Emilie Lecomte
,
Aurélien Guy-Duché
,
Sylvie Saleun
,
Alain Roulet
et al.
20. Annual Meeting of the American-Society-of-Gene-and-Cell-Therapy (ASGCT) , May 2017, Washington, United States
Conference papers
hal-01607265v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Forelimb Treatment in a Large Cohort of Dystrophic Dogs Supports Delivery of a Recombinant AAV for Exon Skipping in Duchenne Patients
Caroline Le Guiner
,
Marie Montus
,
Laurent Servais
,
Yan Cherel
,
Virginie François
et al.
Journal articles
inserm-02447482v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Accurate Identification and Quantification of DNA Species by Next-Generation Sequencing in Adeno-Associated Viral Vectors Produced in Insect Cells
Magalie Penaud-Budloo
,
Emilie Lecomte
,
Aurélien Guy-Duché
,
Sylvie Saleun
,
Alain Roulet
et al.
Journal articles
hal-01608396v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNA
Jean-Baptiste Dupont
,
Benoit Tournaire
,
Christophe Georger
,
Béatrice Marolleau
,
Laurence Jeanson-Leh
et al.
Journal articles
inserm-01799048v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Vitrectomy Before Intravitreal Injection of AAV2/2 Vector Promotes Efficient Transduction of Retinal Ganglion Cells in Dogs and Nonhuman Primates
Kizito-Tshitoko Tshilenge
,
Baptiste Ameline
,
Michel Weber
,
Alexandra Mendes-Madeira
,
Steven Nedellec
et al.
Journal articles
inserm-01799021v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Herpes Simplex Virus Type 1 ICP0 Protein Mediates Activation of Adeno-Associated Virus Type 2 rep Gene Expression from a Latent Integrated Form
Marie-Claude Geoffroy
,
Alberto Epstein
,
Estelle Toublanc
,
Philippe Moullier
,
Anna Salvetti
et al.
Journal articles
hal-03083404v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Adeno-Associated Virus Vector (AAV) microdystrophin gene therapy prolongs survival and restores muscle function in the canine model of Duchenne Muscular Dystrophy (DMD)
Caroline Le Guiner
,
Laurent Servais
,
Marie Montus
,
Thibaut Larcher
,
Bodvael Fraysse
et al.
Conference papers
hal-01602361v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Efficient intrathymic gene transfer following in situ administration of a rAAV serotype 8 vector in mice and nonhuman primates.
Aurélie Moreau
,
Rita Vicente
,
Laurence Dubreil
,
Oumeya Adjali
,
Guillaume Podevin
et al.
Journal articles
hal-00420211v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
NGS library preparation may generate artifactual integration sites of AAV vectors
Benjamin Cogné
,
Richard Snyder
,
Pierre Lindenbaum
,
Jean-Baptiste Dupont
,
Richard Redon
et al.
Journal articles
inserm-01800006v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
RNA-Seq Analysis of an Antisense Sequence Optimized for Exon Skipping in Duchenne Patients Reveals No Off-Target Effect
Claire Domenger
,
Marine Allais
,
Virginie François
,
Adrien Leger
,
Emilie Lecomte
et al.
Journal articles
inserm-01734756v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More
Early Detection of a Two-Long-Terminal-Repeat Junction Molecule in the Cytoplasm of Recombinant Murine Leukemia Virus-Infected Cells
Fatima Serhan
,
Magalie Penaud
,
Caroline Petit
,
Thierry Leste-Lasserre
,
Stéphane Trajcevski
et al.
Journal articles
hal-03140785v1
Actions
Share
Gmail
Facebook
Twitter
LinkedIn
More