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authFullName_s : Severine Pouillot

Transposon-Based, Targeted Ex Vivo Gene Therapy to Treat Age-Related Macular Degeneration (TargetAMD)

Gabriele Thumann , Maria Perdikomati-Dahmen , Zsuzsanna Izsvak , Zoltan Ivics , Alfredo Garcia Layana et al.
Human gene therapy. Clinical development, 2015, 26 (2), pp.97-100. ⟨10.1089/humc.2015.2519⟩
Journal articles hal-03292699v1
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Preclinical Evaluation of a Cell-Based Gene Therapy Using the Sleeping Beauty Transposon System in Choroidal Neovascularization

Maria Hernandez , Sergio Recalde , Laura Garcia-Garcia , Jaione Bezunartea , Csaba Miskey et al.
Molecular Therapy - Methods and Clinical Development, 2019, 15, pp.403-417. ⟨10.1016/j.omtm.2019.10.013⟩
Journal articles hal-03292059v1